Miks haruldaste haiguste ravimid on kallid

Miks haruldaste haiguste ravimid on kallid

EN

Why are medicines for rare diseases expensive

Ravimid annavad lootust haigetele inimestele. Ravimite tegemine maksab palju raha. Seepärast on ravimid kallid.
EN

Medicines give hope to sick people. Making medicines costs a lot of money. That's why medicines are expensive.

Sebastian on 10-aastane poiss. Tal on raske haigus. Uus ravim võib aidata, kuid see maksab 2,5 miljonit eurot.
EN

Sebastian is a 10-year-old boy. He has a serious illness. A new medicine might help, but it costs 2.5 million euros.

Ravim Elevidys võib olla ohtlik. Kolm inimest on surnud selle tõttu. Ravim ei näita head tulemust patsientidel.
EN

The medicine Elevidys can be dangerous. Three people have died because of it. The medicine does not show good results in patients.

USA ravimiamet on . Nad arvasid, et ravim aitab lihastele.
EN

The US drug agency has approved the medicine. They thought the medicine would help the muscles.

Ravimite hind on kõrge, sest nende tegemine on pikk ja kallis. Haruldaste haiguste ravimeid kasutab vähe inimesi.
EN

The price of medicines is high because their production is long and expensive. Few people use medicines for rare diseases.

Elevidys on . See kasutab viirust, mis aitab lihastele. Ravimile võib efekti olla mitu aastat.
EN

Elevidys is a gene therapy. It uses a virus that helps the muscles. The medicine may take several years to show effects.